Therapeutic Potential

Arrakis’s transformative approach to small-molecule drug discovery enables targeting RNA and opens up a vast new domain for discovering new medicines.

The human transcriptome, the set of all RNAs transcribed from DNA, is hundreds of times larger than the set of protein drug targets, and its therapeutic potential remains largely unexplored. Arrakis’s unique science will open all of the transcriptome to therapeutic intervention by small molecules, dramatically expanding the universe of opportunities for new drug discovery and new treatments for patients.

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